Lumry, William R.
Zuraw, Bruce
Cicardi, Marco
Craig, Timothy
Anderson, John
Banerji, Aleena
Bernstein, Jonathan A.
Caballero, Teresa
Farkas, Henriette
Gower, Richard G.
Keith, Paul K.
Levy, Donald S.
Li, H. Henry
Magerl, Markus
Manning, Michael
Riedl, Marc A.
Lawo, John-Philip
Prusty, Subhransu
Machnig, Thomas
Longhurst, Hilary
,
Funding for this research was provided by:
CSL Behring
Article History
Received: 5 February 2020
Accepted: 22 December 2020
First Online: 15 February 2021
Change Date: 28 July 2021
Change Type: Correction
Change Details: A Correction to this paper has been published:
Change Details: https://0-doi-org.brum.beds.ac.uk/10.1186/s13023-021-01975-2
Ethics approval and consent to participate
: The study protocol and amendments were approved by independent ethics committees or institutional review boards at all participating centers prior to study commencement. All participants and/or a parent/guardian (where applicable) provided written informed consent prior to participation in the study.
: Not applicable.
: W Lumry is a consultant for Adverum, Attune, BioCryst, CSL Behring, Kalvista, Pharming, and Takeda; a speaker for CSL Behring, Pharming, and Takeda; and has received research grants from BioCryst, CSL Behring, Pharming, Ionis, and Takeda. B Zuraw has served as a consultant for Adverum, Attune, BioCryst, CSL Behring, and Takeda. M Cicardi was a PI, consultant, and speaker for CSL Behring, Shire/Takeda, and Pharming; a consultant PI for BioCryst, Kalvista, Attune, and Pharvaris; and conducted research with Pharming and Shire/Takeda. T Craig is a consultant and speaker for CSL Behring, Shire/Takeda, Spark, and Pharming; has conducted research for CSL Behring, Shire/Takeda, Ionis, and BioCryst; and is on the Medical Advisory Board for the HAEA, Board of Directors for the AAAAI and the Board of Directors for ALA- Mid Atlantic. J Anderson is a PI, consultant, and speaker for CSL Behring, Shire/Takeda, and Pharming and a PI for BioCryst. A Banerji conducted research with Shire/Takeda, BioCryst and served as a consultant for Shire/Takeda, BioCryst, Pharming, CSL, and Kalvista. JA Bernstein is a PI, consultant, and speaker for CSL Behring, Shire/Takeda, and Pharming; a consultant and PI for BioCryst; and a consultant for Kalvista. T Caballero is a speaker for CSL Behring, Merck, Novartis, and Shire/Takeda; consultant for BioCryst, CSL Behring, Novartis, Octapharma, Pharming, and Shire/Takeda; she has been a PI in clinical trials/registries for BioCryst, CSL Behring, Novartis, Pharming, and Shire/Takeda; she has received educational funding from CSL Behring, Novartis, and Shire/Takeda; and she is a researcher from the IdiPAZ program for promoting research activities. H Farkas has received honoraria, speaker fees, and travel grants from CSL Behring, Shire/Takeda, Swedish Orphan Biovitrum, and Pharming and/or served as a consultant for these companies and has participated in clinical trials/registries for BioCryst, CSL Behring, Pharming, and Shire/Takeda. RG Gower has conducted research with Shire/Takeda and BioCryst; he has served as a consultant with Shire/Takeda and CSL Behring; is on the advisory board for Shire/Takeda, BioCryst, and Fresenius Kabi; and he has received speakers’ fees from Shire/Takeda. PK Keith has conducted research with, served as a consultant for, and has received speakers’ fees from Shire/Takeda and CSL Behring. DS Levy has served as a consultant, speaker, and has received research grants from CSL Behring; he has served as a consultant for BioCryst; he has served as a speaker for Takeda. HH Li has conducted research with and has served as a consultant/received speakers’ fees from Shire/Takeda, BioCryst, and CSL Behring; he has served as a consultant/received speakers’ fees from Pharming. M Magerl is a PI, consultant, and/or speaker for CSL Behring, BioCryst, Kalvista, Shire/Takeda, and Pharming. M Manning is a researcher/PI and speaker/consultant at CSL Behring, Shire/Takeda, BioCryst, and Pharming. M Riedl is a research investigator with CSL Behring, Takeda, BioCryst, and Ionis; he has served as a consultant for CSL Behring, Takeda, BioCryst, Pharming, Adverum, Attune, Kalvista, and Pharvaris; and he has received speakers’ fees from CSL Behring, Takeda, and Pharming. J-P Lawo, S Prusty, and T Machnig are/were employees of and stockholders at CSL Behring during study conduct. H Longhurst served as a consultant for, participated in research with or accepted educational funding support from Adverum, BioCryst, CSL Behring, GSK, Kalvista, Pfizer, Pharming, Pharvaris, and Shire/Takeda.